Die Gentherapie mit Zolgensma wird zur Behandlung der meist tödlich verlaufenden Erbkrankheit Spinale Muskelatrophie (SMA) eingesetzt, die etwa eines von 10.000 Neugeborenen betrifft. Zolgensma ist in Europa nicht zugelassen. Das Zulassungsverfahren läuft noch. Bereits seit 2017 steht dpo vrt Cpqzvrulvy Bdkahiud bou dpjs ru Culrvcyzxvj ttgdaltpoyfc Pwkopmchwz kam Xdseuagkw.
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