Für die meisten Patienten bedeutet eine neuromuskuläre Erkrankung immer noch den fortschreitenden Verlust der Bewegungsfähigkeit. Neu entwickelte Behandlungsmöglichkeiten und der Einsatz neuer Gentherapien sind das große Thema der 25. Jahrestagung des Medizinisch-Wissenschaftlichen Beirates der Deutschen Gesellschaft für Muskelkranke e. V. (DGM). Diese findet vom 24.-27. März 2021 digital statt. Mit der aktuellen Diskussion der Gentherapien und den damit verbundenen neuen Chancen zur Behandlung neuromuskulärer Erkrankungen legt Tagungspräsident PD Dr. med. Julian Großkreutz, Jena, den Fokus auf die wissenschaftlichen, medizinischen und gesellschaftlichen Herausforderungen, die die Verfügbarkeit der hochwirksamen neuen Therapien für neuromuskuläre Patienten bedeutet. Im Interview gibt er erste Einblicke in Ndnenkpotidk djo Ucrkhyopjc aug Pnrmhd.
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